Tag Archives: SickleCell

These Patients Had Sickle-Cell Disease. Experimental Therapies Might Have Cured Them.

Scientists have long known what causes sickle-cell disease and its devastating effects: a single mutation in one errant gene. But for decades, there has been only modest progress against an inherited condition that mainly afflicts people of African descent. With advances in gene therapy, that is quickly changing — so much so that scientists have… Read More »

Global Health: ‘From Nothing to Gangbusters’: A Treatment for Sickle-Cell Disease Proves Effective in Africa

A drug that protects children in wealthy countries against painful and sometimes lethal bouts of sickle-cell disease has been proven safe for use in Africa, where the condition is far more common, scientists reported on Saturday. More research remains to be done, experts said, but knowing that hydroxyurea — a cheap, effective and easy-to-take pill… Read More »