Tag Archives: Therapy

FDA Approves Zolgensma (onasemnogene abeparvovec-xioi) Gene Therapy to Treat Pediatric Patients with Spinal Muscular Atrophy

FDA Approves Zolgensma (onasemnogene abeparvovec-xioi) Gene Therapy to Treat Pediatric Patients with Spinal Muscular Atrophy Print this page May 24, 2019 — The U.S. Food and Drug Administration today approved Zolgensma (onasemnogene abeparvovec-xioi), the first gene therapy approved to treat children less than two years of age with spinal muscular atrophy (SMA), the most severe… Read More »

Light Therapy, Anyone?

I have a beef with the insurance industry. According to the Social Security Administration, I’ve been disabled due to my Major Depressive Disorder (MDD) since August 29, 2005. (Yes, I know – that’s a long fucking time.) For those of you not in-the-know, after two years of being on Social Security Disability (aka SSDI, which… Read More »

Second death in Novartis gene therapy trials under investigation

(Reuters) – Novartis AG, which this week announced positive interim trial results for its experimental gene therapy for spinal muscular atrophy, on Friday said investigation is underway into whether a second trial death could be related to the treatment. The logo of Swiss drugmaker Novartis AG is seen at its headquarters in Basel, Switzerland January… Read More »